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European Patent (TR Translation)

Antisens Nükleik Asit.

Invention Abstract

İnsan distrofin geninde ekzon 51'in yüksek verimli bir şekilde atlanmasına olanak sağlayan bir ilaç sağlanmaktadır. Mevcut buluş, insan distrofin geninde ekzon 51'in atlanmasını sağlayan bir antisens oligomeri sağlamaktadır.

IPC Classes
C12N 15/09A61P 21/00A61K 31/7125A61K 31/712A61K 31/711C12N 15/113
Parties
Inventor
Tatsushı Wakayama C/O Nippon Shinyaku Co. Ltd. 14-1 Sakura 3-Chome Tsukuba-Shi Ibaraki 305-0003 / Japonya Haruna Seo C/O Nippon Shinyaku Co. Ltd. 8-4 Nihonbashi 3-Chome Chuo-Ku Tokyo 103-0027 / Japonya Tetsuya Nagata C/O National Center Of Neurology And Psychiatry 1-1 Ogawahigashi-Cho 4-Chome Kodaira-Shi Tokyo 187- 8551 / Japonya Shın'ıchı Takeda C/O National Center Of Neurology And Psychiatry 1-1 Ogawahigashi-Cho 4-Chome Kodaira-Shi Tokyo 187- 8551 / Japonya Youheı Satou C/O Nippon Shinyaku Co. Ltd. 14-1 Sakura 3-Chome Tsukuba-Shi Ibaraki 305-0003 / Japonya
Rights Holder
Nıppon Shınyaku Co., Ltd. 14, Kisshoin Nishinosho Monguchicho Minami-Ku Kyoto-Shi Kyoto 601-8550 / Japonya Natıonal Center Of Neurology And Psychıatry 4-1-1, Ogawahigashi-Cho Kodaira-Shi Tokyo 187-8551 / Japonya
Attorney
Filiz Ark (Mumcuoğlu Ve Ark Patent Ve Marka Dan. Ltd. Şti.) Mutlukent Mah. Mutluköy Sitesi 1943. Cad. No:10 06800 - Çankaya/Ankara

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